Duchenne muscular dystrophy families are sharing stories about Elevidys complications on social media. But they aren’t ...

The death of a boy with Duchenne muscular dystrophy, tied to a gene therapy, is above all a tragedy. But it is also ...

In this week’s edition of InnovationRx, we look at the dangers of RFK Jr.’s vaccine advisory committee, how Trump’s visa ban ...

In another tragic incident, Sarepta Therapeutics (NASDAQ: SRPT) saw a second death in connection with its Duchenne muscular ...

The most talked about and market moving research calls around Wall Street are now in one place. Here are today’s research ...

The most talked about and market moving research calls around Wall Street are now in one place. Here are today's research calls that investors need to know, as compiled by The Fly. Top 5 Upgrades: ...

I am upgrading Dyne Therapeutics stock to a 'Buy' rating due to promising late-stage DM1 and DMD drug candidates and ...

Many parents said they were afraid of noninvasive ventilation, with some citing inaccurate concerns about ventilation devices.

CSL Behring’s Andembry is now approved as a subcutaneous, self-injection for hereditary angioedema (HAE) patients ages 12 and older and will be available by the end of June 2025.

President Javier Milei's severe budget cuts to Argentina's public health system have led to a decline in care, particularly affecting cancer patients, according to experts, government workers and ...