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MedPage Today on MSN8d
Bone Health in Duchenne Muscular Dystrophy
An alternative to using standard glucocorticoids is the synthetic dissociative steroid vamorolone (Agamree), which was ...
Cell therapy prevents damage from Duchenne muscular dystrophy in mouse model
A cell therapy preserves muscle structure and function in laboratory mice with a type of disease similar to Duchenne muscular ...
Doncaster teacher takes on cycling challenge for son living with muscular dystrophy
On Saturday 12 July, Claire Ellis, 34, a teacher from Doncaster set off from her home to cycle 100km in support of her son ...
Doncaster Free Press on MSN12h
Mum's cycling challenge fundraising for ‘Declan’s Muscle Mission’ inspired by son, 11, who lives with Duchenne muscular dystrophy
Last month Claire Ellis, aged 34, a teacher from Doncaster, set off from her home to cycle 100km in support of her son Declan ...
Tennessee boy channels 'The Flash' in race to cure Duchenne muscular dystrophy
A 12-year-old boy from Carthage, Tennessee finds joy in his power wheelchair. His family are hoping for a cure for his muscular disease, Duchenne.
Hyderabad teen with muscular dystrophy shines at international chess championship
K.S.R.A. Praneeth, an 18-year-old battling Duchenne Muscular Dystrophy, competed in the World IPCA Chess Championship in Goa, ...
Townsville Bulletin3d
Community rallies behind teen with Duchenne Muscular Dystrophy, raising $12,000 in short time
A teenager living with a severe and degenerative condition is hoping to retain his independence in the face of the cruel ...
FDA’s Reversal on Gene Therapy Helps My Son
Parents of boys with Duchenne muscular dystrophy weigh in on drug innovation and medical regulation.
FDA Suspends Muscular Dystrophy Drug After 3 Patient Deaths
The U.S. Food and Drug Administration ( FDA) has placed an immediate clinical hold on Sarepta Therapeutics' investigational ...
STAT12d
FDA permits use of Sarepta Therapeutics’ Duchenne therapy in younger patients after short-lived halt
The FDA said it was clearing the way for Sarepta Therapeutics to resume shipments of its gene therapy for Duchenne muscular ...
Dyne Therapeutics Announces FDA Breakthrough Therapy Designation for DYNE-251 in Duchenne Muscular Dystrophy (DMD)
Dyne Therapeutics, Inc. (Nasdaq: DYN), a clinical-stage company focused on delivering functional improvement for people living with genetically driven neuromuscular diseases, today announced that the ...
The American Journal of Managed Care9d
FDA Recommends Sarepta Resume DMD Gene Therapy Shipments for Ambulatory Patients
Shipment of delandistrogene moxeparvovec, a gene therapy for Duchenne muscular dystrophy (DMD), will resume following a ...