Thousands of years ago, a special child was born in the Sahara. At the time, this was not a desert; it was a green belt of savannas, woodlands, lakes and rivers. Bands of hunter-gatherers thrived ...

Exa-cel, a new CRISPR-based treatment, modifies the genes of the patient's stem cells to induce them to produce fetal hemoglobin. I have a long-standing interest in sickle cell anemia, a genetic ...

Dr. Vernon Rayford, an internal medicine specialist and pediatrician from Tupelo, Miss., says St. Jude Children’s Research Hospital is actively examining a cure for sickle cell anemia. As a St. Jude ...

ROANOKE, Va. – Ensuring no one fights alone. The Carilion Clinic Sickle Cell Collaborative is holding a walk to honor sickle cell patients and their caregivers on Saturday. Sickle cell disease is a ...

UCSF Benioff Children's Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell disease. The trial is the first in the U.S. to apply non-viral CRISPR-Cas9 ...

Both new FDA-approved medicines offer a potential cure, but they will come with a hefty price tag and it will be years before their long-term effects are clear. Sickle cell disease, a painful ...

The first gene therapies approved to treat sickle cell disease in December 2023 are struggling on the market. But there are glimpses of forward momentum as Vertex and Genetix Bio provide updates.

He's the first in New York to receive the novel treatment and one of the first in the world. Share on Facebook (opens in a new window) Share on X (opens in a new window) Share on Reddit (opens in a ...

Sickle cell disease (SCD) is a genetic condition that affects more than 8 million people worldwide by altering the shape of oxygen-carrying red blood cells. Normally, red blood cells are shaped like ...