Regulatory flexibility can be exercised in rare disease without sacrificing rigor,” writes Mindy Leffler, whose son has ...

Capricor Therapeutics is trying to stave off FDA rejection of its cell therapy for Duchenne muscular dystrophy.

Dystrophy is any condition in which a part of the body weakens or wastes away. In muscular dystrophy, the weakness is in the muscles. An inherited genetic mistake prevents the body from making a ...

For Duchenne and Becker muscular dystrophies, muscle biopsy may show whether dystrophin, a muscle protein, is missing or abnormal, and DNA testing is used to analyze the condition of the related gene.

Binghamton researchers show the drug Vamorolone can treat very young boys with Duchenne muscular dystrophy, preventing muscle loss.

Deramiocel can safely slow the progression of advanced Duchenne muscular dystrophy among people aged 10 years and older.

The Jett Foundation donated the van to Beckham Kendall's family.

Muscular dystrophy, a condition that affects the body's muscles, comes with progressive muscle weakness and prolonged periods of muscle tightness. An estimated 975,000 to 3 million people worldwide ...

Muscular dystrophy is a debilitating disease that causes the weakness and breakdown of skeletal muscles that progressively worsens over time. According to a team of University of Maine researchers, ...

Tributes poured in for Gilbert Gottfried on Tuesday after news broke that he died in Manhattan. The 67-year-old comedian’s family shared on Twitter that he passed away “after a long illness.” ...